TIMBERLINE study shows good safety and sweat chloride reductions with triple combo CFTR mo ...
A methylation marker on the tRNA, and a new lipid nanoparticle, helps the ribosome ignore disease-causing mutations ...
Ride Therapeutics (´Ride´or ´the Company´), an engineering and machine learning powered biotechnology company committed to solving the delivery challenge for genetic medicines, today announced a ...
Aptar's ACT-101 is designed to intervene a step earlier than current CF modulators.
NOVA has announced THE BATTLE TO BREATHE, a new documentary chronicling the decades-long effort that led to a breakthrough ...
Breathing disorders are common in the U.S. with conditions like COPD affecting some 7% of the population and asthma affecting another 10%. Digestive conditions like GERD, acid reflux, Celiac disease ...
Cystic fibrosis, one of the most common genetic diseases in Switzerland, promotes chronic bacterial infections by impairing ...
Cystic fibrosis is an inherited condition that can cause mucus buildup in the pancreas. This can interfere with the typical pancreas function and cause problems during food digestion. It can also ...