If approved, UX111 will be the first approved therapy for the treatment of Sanfilippo syndrome Type A, a rare disease affecting young children ...

Denali Therapeutics solved a major challenge in Hunter syndrome treatment. Now it's ready to take its technology further.

Patients in the EU with rare disease thymidine kinase 2 deficiency (TK2d) have their first approved therapy, UCB's Kygevvi, ...

Serum levels of B vitamins don't adequately reflect nutritional state for patients with chronic kidney disease (CKD).

FitIndiaHitIndia: Know the best exercises to reduce fatty liver naturally, improve metabolism, support weight loss, and boost overall liver health with simple, effective daily routines.

Proteins are one of the most essential nutrients for the human body and form an integral part of a balanced diet. They are important for body structure, proper functioning, and muscle strength.

Many people never think about the fact that most food contains histamines. And, for the most part, the body is able to break ...

Phase 2b POLAR study, a global, randomized, double-blind, placebo-controlled clinical trial evaluating GLM101 for the ...

Welcome to another installment of This Week at FDA, your weekly source for updates – big and small – on FDA, drug, and medical device regulation and what we’re reading from around the web. This week, ...

From cruciferous vegetables to extra-virgin olive oil, here’s what to eat for the health of one of your most important organs.

The FDA has approved Kresladi, the first gene therapy for severe Leukocyte Adhesion Deficiency Type I. Designed for pediatric patients without a suitable donor, the therapy modifies a patient’s own ...

Findings suggest that impaired fiber metabolism in celiac disease is due to microbial deficits, not just diet, emphasizing ...