Medscape

Sickle Cell Disease in Oman: Lessons for the Rest of the World

A specialist from Oman, located at the crossroads of Africa and Asia, explains that his nation serves as a microcosm when it ...

Zydus gets USFDA's orphan drug designation for beta-thalassemia product

Zydus Lifesciences announced a significant development for beta-thalassemia patients. The US Food and Drug Administration has ...

Vertex’s Cystic Fibrosis Sales Beat, as Newer Drugs Miss

Vertex Pharmaceuticals Inc. reported third-quarter sales that beat analysts’ expectations as the biotech company’s mainstay ...

Vertex beats quarterly estimates on cystic fibrosis demand, new drugs

Vertex Pharmaceuticals reported on Monday that it beat Wall Street estimates for third-quarter results, driven by strong demand for its cystic fibrosis treatments and early contributions from newer ...
Yahoo Finance

Genetix Biotherapeutics to Present Recent Patient Experience Data from U.S. Commercial Gene Therapy Implementation at the 67th American Society of Hematology (ASH) Annual Meeting

said Joanne Lager, MD, Chief Medical Officer. "The presentation highlights the growing demand for ZYNTEGLO, the first FDA-approved gene therapy for eligible patients with transfusion-dependent ...