Vertex Pharmaceuticals (Nasdaq: VRTX) announced today a reimbursement agreement with NHS England for eligible sickle cell disease (SCD) patients to access the CRISPR/Cas9 gene-edited therapy, CASGEVY® ...
Non-transfusion-dependent thalassemia encompasses three clinically distinct forms -- beta-thalassaemia intermedia, hemoglobin ...
YolTech Therapeutics, a clinical-stage gene editing company dedicated to delivering lifelong cures, announced the initiation of a clinical trial for YOLT-204, an investigational therapy for the ...
The expression of fetal hemoglobin has the potential to normalize hemoglobin composition and the red blood cell counts in patients with transfusion-dependent beta-thalassemia, eventually making them ...
Apple has just released new beta software for Mac and Vision Pro. macOS Sequoia 15.3 and visionOS 2.3 beta 3 are rolling out now for users with a developer account. Update: macOS 15.3 beta 3 is ...
The Elden Ring Nightreign beta test has been revealed for February 2025 and registrations to potentially be a part of it are now open! During this test, if you've been selected, you'll be able to ...
Apple has released a new beta 3 update. Just hours after the recent debut of beta 3 for tvOS and HomePod only, watchOS 11.3 has received its beta 3 update too. New beta brings software updates clo ...
The year 2025 marks a generational shift: children born between January 1, 2025, and December 31, 2039, will comprise Generation Beta. This generation succeeds Generation Alpha, also dubbed the iPad ...
You probably had a hemoglobin electrophoresis test done at some point to make the diagnosis of beta thalassemia minor, so this would be useful to present to new doctors. Making a definitive ...