While recent FDA guidance speaks to the agency’s support of innovative trial designs—including the use of external ...
A 7-year-old girl can hear her mom's voice again, thanks to a radical gene therapy. Scientists just proved hereditary ...
For many people born with hearing loss, the world has always been quiet. This type of hearing problem, known as congenital ...
The act of swallowing changes as people age and can make holiday treats like Easter candy difficult for older adults to ...
A groundbreaking gene therapy trial has successfully restored hearing in individuals with a rare form of congenital deafness.
UF scientist develops safer gene therapy restoring vision in children with rare inherited eye diseases; pivotal trials begin ...
In Alzheimer’s disease, brain damage is often linked to a mix of problems, including beta-amyloid buildup, tau pathology, ...
A new gene therapy is giving people born deaf the chance to hear, often within just weeks. In a small but groundbreaking ...
Two Louisiana parents, Charles and Curtshandra Duplechain, are helping raise awareness for INAD, a rare genetic condition ...
After years of hospital stays, these kids are thriving thanks to a gene therapy that just earned accelerated FDA approval.