Nearly one in three people with cystic fibrosis experienced nephrolithiasis during their lifetime. 2. The degree of exocrine pancreatic insufficiency control was not associated with nephrolithiasis. 3 ...
In this open-label phase 1–2 study, pediatric patients with mucopolysaccharidosis type II treated with tividenofusp alfa showed substantial reductions in cerebrospinal fluid and urinary heparan ...